The first multidisciplinary peer-reviewed fully open access ejournal in child neurology

Published: May 31, 2019

Position Statement:Emerging genetic therapies for rare disorders

Genetic therapies

Pauline Samia, Adam Kirton, Russell Dale, Silvia Tenembaum, Chahnez Charfi Triki, Anaita Hegde, Richard Idro, Edward Kija, Jo M Wilmshurst, Ingrid Tein, Haluk Topaloğlu
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